一本快速出版的同行評審的雜志，涵蓋了人類基因治療的所有方面。發表關于包括人類在內的哺乳動物基因轉移和表達的原始研究的科學論文。介紹了在媒介發育、傳遞系統和動物模型方面的改進，特別是在癌癥、心臟病、病毒性疾病、遺傳疾病和神經系統疾病方面的改進。包括與人類基因轉移領域直接相關的倫理/法律/監管文件。

A rapid-publication peer-reviewed journal covering all aspects of human gene therapy. Publishes scientific papers on original investigations into the transfer and expression of genes in mammals, including humans. Improvements in vector development, delivery systems, and animal models, particularly in the areas of cancer, heart disease, viral disease, genetic disease, and neurological disease, are covered. Includes ethical/legal/regulatory papers related directly to the area of gene transfer into humans.